Tag Archives: gene therapy
The Genetic Medicine Revolution — Eyes on the Future
Is the genetic revolution everybody talked about in 2001 after the human genome sequencing, here already? History and Background: It is astounding that as early as the 1960s, scientists speculated that DNA sequences could be introduced into
Dramatically distinct tropism and transduction efficiencies of AAV serotypes following subconjunctival injection
Instead of relying on traditional drug modalities, gene therapies rely on delivery of nucleic acids into patient’s cells to prevent, slow, stop or treat diseases. In the past decades, gene therapy has been broadly studied in pre-clinical
Hearing the light: Improved frequency resolution of optical vs. electrical inner ear stimulation
Auditory signals, including human speech, are characterized by many features, one important being sound frequency, which is perceived as pitch. In normal hearing people, the cochlea in the inner ear translates different sound frequencies into neural activation
A versatile in vitro bioassay for the screening of neurotrophic factor gene therapy systems to combat blindness
Glaucoma is the world’s second leading cause of blindness after cataracts, affecting about 80 million people worldwide annually. The disease is characterized by neurodegeneration involving a progressive visual field loss from the periphery towards the center, and
Gene therapy: a promising candidate for cystic fibrosis treatment
An improved gene therapy treatment can cure mice with cystic fibrosis (CF). Cell cultures from CF patients, too, respond well to the treatment. Those are the encouraging results of a study presented by the Laboratory for Molecular
